Rare Blood Disorders
Explore facts and recommendations for pharmacological treatments for rare blood disorders.
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Risk Mitigation During Concizumab Prophylaxis in Phase 3 Clinical Trials in Patients With Hemophilia A/B With and Without Inhibitors
This poster reviews the risk mitigation strategy and breakthrough bleed management guidance for patients treated with concizumab in clinical trials.
Improved Quality of Life and Satisfaction With N8-GP in US Patients
This poster reviews the health-related quality of life and satisfaction in US patients with severe hemophilia A receiving N8-GP in the pathfinder trials.
Longitudinal Efficacy and Safety of N9-GP for Prophylaxis and Bleed Control in US Patients
This poster reviews the efficacy and safety of N9-GP in US patients on prophylactic and on-demand therapy.
Emerging Non-Factor Therapies for Hemophilia
Mechanism of action for emerging therapies to treat hemophilia without using replacement coagulation factor.